by rss feed | Dec 10, 2023 | Casgevy, Lyfgenia, News Feeds, Paolo Macchiarini, Sickle Cell Disease, weekly reads
The big news broke Friday that the FDA approved two new gene therapies for sickle cell disease. While the approvals were expected and the actual use of these treatments will be complex on several levels, this is a historic development. 2 FDA-approved gene therapies...
by rss feed | Jan 9, 2022 | News Feeds, Sickle Cell Disease, weekly reads
Is 2022 going to be any better than 2020 or 2021 when it comes to things in general or for biomedical science? Related to the pandemic? It’s too soon to say but if I had to guess right now I’d venture an optimistic view that overall it’s going to be...
by rss feed | Feb 16, 2021 | biotechs, Bluebird Bio, gene therapy, News Feeds, Sickle Cell Disease
Recently I was going through a list I’m updating of regenerative medicine biotech companies including Bluebird Bio. Now just a few days later the world seems turned upside down for the firm and maybe to some degree for other companies doing related work....
by rss feed | Jan 17, 2021 | CRISPR, CRISPR sickle cell, News Feeds, Parkinson's Disease, Sickle Cell Disease, Weekend Reads, weekly reads
I’m playing catch-up on some reading given how busy I’ve been and this includes a groundbreaking NEJM pub on CRISPR for Sickle Cell and Thalassemia. CRISPR for Sickle Cell From December, here’s the key paper in the NEJM: CRISPR-Cas9 Gene Editing for...
by rss feed | Jan 17, 2021 | CRISPR, CRISPR sickle cell, News Feeds, Parkinson's Disease, Sickle Cell Disease, Weekend Reads, weekly reads
I’m playing catch-up on some reading given how busy I’ve been and this includes a groundbreaking NEJM pub on CRISPR for Sickle Cell and Thalassemia. CRISPR for Sickle Cell From December, here’s the key paper in the NEJM: CRISPR-Cas9 Gene Editing for...
