Can Gene-Edited Stem Cells Treat Cystic Fibrosis?

by | Sep 28, 2020 | Brian R. Davis, CFTR mutation, CRISPR, CRISPR for Cystic Fibrosis, Cystic Fibrosis, Francis Collins, gene editing, Lap-Chee Tsui, News Feeds, Nicholas E. King, Ricki Lewis, scRNA-Seq, Stem cells for cystic fibrosis, the Niche

Drugs that restore the shape of the errant protein behind cystic fibrosis (CF) have, over the past eight years, helped the majority of patients, who have certain mutations. Gene-corrected stem cells might offer a “mutation agnostic” option to CF. CF results from a...